Twins Emma and Bartosz, both diagnosed with Spinal Muscular Atrophy, highlight the urgent need for newborn screening in the UK.


Twins Emma and Bartosz, both diagnosed with Spinal Muscular Atrophy, highlight the urgent need for newborn screening in the UK.

The Forrester family faces the harsh reality of childhood dementia as their daughter Leni battles Sanfilippo disease. They advocate for…